Immusoft Corporation, a cell therapy company dedicated to improving the lives of patients with rare diseases, today announced that it will feature oral and poster presentations at the upcoming ...

Discover Sanfilippo Syndrome a rare genetic disorder affecting childrens development Learn about its symptoms treatment ...

It is a recessive X-linked disease, which means mothers have a 50 per cent chance of passing it to their sons. It is rare and ...

Equities researchers at Cantor Fitzgerald issued their FY2025 earnings per share estimates for Ultragenyx Pharmaceutical in a ...

Jupiter Neurosciences, Inc.’s JUNS share price has dipped by 59.50%, which has investors questioning if this is right time to ...

Stock analysts at Leerink Partnrs lifted their FY2024 EPS estimates for Ultragenyx Pharmaceutical in a report released on ...

Haliza Md Kasim’s eyes widened. Despite having gone through this before with her first son, Yusof, and despite the doctors ...

Nanosonics (ASX:NAN) has achieved a feather duster-to-rooster transformation with a bullish trading update for the December ...

Data from the first patients enrolled into Regenxbio's trial of its gene therapy for rare inherited disease mucopolysaccharidosis type I (MPS I) – also known as Hurler syndrome – has shown the ...

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Perth Zoo's last female elephant has left for her forever home in South Australia. Locals report seeing sparking and smoke near a power transmitter close to Arthur River, where a bushfire ripped ...

Israel’s Cease-Fires in Lebanon and Gaza Appear Fragile Israeli forces killed at least 22 people and injured dozens more in southern Lebanon on Sunday, Lebanese officials said. In Gaza, Israel ...