Discover Sanfilippo Syndrome a rare genetic disorder affecting childrens development Learn about its symptoms treatment ...

When a mother has a faulty gene that causes a disease like Hunter Syndrome on her X chromosome, a son has a 50 percent chance of being affected, while girls have a 50 percent chance of being a carrier ...

Equities researchers at Cantor Fitzgerald issued their FY2025 earnings per share estimates for Ultragenyx Pharmaceutical in a ...

Jupiter Neurosciences, Inc.’s JUNS share price has dipped by 59.50%, which has investors questioning if this is right time to ...

Stock analysts at Leerink Partnrs lifted their FY2024 EPS estimates for Ultragenyx Pharmaceutical in a report released on ...

Haliza Md Kasim’s eyes widened. Despite having gone through this before with her first son, Yusof, and despite the doctors ...

Nanosonics (ASX:NAN) has achieved a feather duster-to-rooster transformation with a bullish trading update for the December ...

Data from the first patients enrolled into Regenxbio's trial of its gene therapy for rare inherited disease mucopolysaccharidosis type I (MPS I) – also known as Hurler syndrome – has shown the ...

With a full-blown land war in Ukraine and an isolationist American president back in the White House, European leaders have come to a stark conclusion: They must spend more on their militaries ...

The releases of the hostages and around 200 prisoners were the second exchange as part of the cease-fire deal in Gaza. Israel said the four hostages, all women, were back in the country. President ...