"My daughters are definitely my biggest inspiration- and the desire to affect change and make the world a better place for them is the driving force behind what I do." ...

Rett syndrome is a rare neurodegenerative disorder that almost exclusively affects girls. It is typically diagnosed in babies between six and 18 months of age, when the first symptoms begin to appear.

Neurogene ( ($NGNE) ) just unveiled an update. On November 6, 2025, Neurogene Inc. announced the dosing of the first participant in the Embolden™ ...

Down syndrome is caused by an error in cell division during development. Individuals receive three copies of chromosome 21 instead of the typical two copies, resulting in duplicates of the genes ...

Taysha Gene Therapies has regained full rights to TSHA-102, its program that is in clinical evaluation to treat the neurodevelopmental disease Rett syndrome. Taysha had in 2022 granted the ...

Taysha Gene Therapies Inc. (NASDAQ:TSHA) is one of billionaire Steve Cohen’s small-cap stock picks with huge upside potential. On October 20, Raymond James initiated coverage on Taysha Gene Therapies ...

Wayne and Coleen Rooney looked happier than ever as they cosied up to their four sons wearing matching Christmas pyjamas in a ...

For the second time, Astellas is walking away from Taysha Gene Therapies, this time choosing not to license the biotech’s adeno-associated-virus-based therapy designed to treat a rare ...

Dozens of people testified at the state Capitol in support of a bill to legalize medical marijuana in Wisconsin. The bill, introduced by Republicans, would create a tightly regulated program for ...

OMAHA, Neb. (WOWT) - It’s through listening and studying music that James or “boby” can just be himself. It can also help when dealing with the loss of his parents. Though he can’t always verbalize it ...

Kentucky gets Gators at Kroger Field in what will be Florida’s first true road game under their interim head coach.