Not necessarily a band name you want to go around recommending to people willy-nilly, but music worth recommending ...

The US FDA has tightened the use of a Duchenne muscular dystrophy gene therapy after two teenage patients died from acute ...

Elevidys now carries a black box warning for acute liver injury and failure, limiting its use to ambulatory patients aged four and older. The FDA's actions follow fatal liver failure reports in ...

DC's "Absolute Batman" comic book series not only offers readers a new take on Bruce Wayne, but also several famous members ...

Ascendis Pharma A/S (Nasdaq: ASND) today announced that pivotal Week 52 results from its randomized double-blind, ...

Shanghai Henlius Biotech, Inc. (2696.HK), and Organon today announced that the US Food and Drug Administration (FDA) has approved the Biologics License Application (BLA) for POHERDY® (pertuzumab-dpzb) ...

Sarepta Therapeutics, Inc., the leader in precision genetic medicine for rare diseases, announced an update to the prescribing information for Elevidys (delandistrogene moxeparvovec-rokl), the only ...

Erik Voss dives deep into this fourth episode of Skeleton Crew to point out all the references to Star Wars and other cool Easter Eggs and details you missed! Become a member to get access to perks: ...

New York City Mayor-elect Zohran Mamdani says he hopes to meet with President Donald Trump to find ways the political polar opposites can work together on the central focus of his winning ...

The indication was restricted to only patients with DMD who are 4 years of age and older with a confirmed mutation in the DMD gene; the indication for non-ambulatory patients with DMD was removed.

System of Care to Advance Care for the Most Commonly Inherited Heart Disease ...

On a hilltop in east-central Poland, archaeologists have found an unusual Iron Age tool: an iron scalpel, likely once ...