A new class of life-saving drugs is helping children who once had no hope. But some carry a price tag of millions for a ...
A mom was overjoyed when she learned a gene therapy treatment could save her child's life, until she found out no one would ...
Revolutions in gene therapy are rapidly changing the landscape of modern medicine, forcing society and science alike to ...
The U.S. Food and Drug Administration said on Tuesday it had approved the first gene therapy for a rare and life-threatening ...
FDA approves 1st gene therapy for Wiskott-Aldrich syndrome, offering a new treatment for patients lacking matched stem cell donors.
A new class of life-saving drugs is helping children who once had no hope. But some carry a price tag of millions for a ...
The FDA has granted approval to a new gene therapy for a rare immune disorder, the maker of which is notably not a drug ...
Zevaskyn, the first gene therapy for recessive dystrophic epidermolysis bullosa, showed significant wound healing in phase 3 ...
The FDA has issued its stamp of approval to a new, cell-based option to treat Wiskott-Aldrich syndrome (WAS), marking the ...
The patchwork rollout of a gene therapy exposes weaknesses in the pricing and regulatory frameworks that determine who ...
To our immune system, a potentially lifesaving gene therapy can look a lot like a dangerous infection. That's because most ...
NEW YORK and TRUMBULL, Conn., April 30, 2025 /PRNewswire/ -- Apertura Gene Therapy, a biotechnology company focused on innovative gene therapy solutions, and the Rett Syndrome Research Trust (RSRT), ...
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